1.
Dorit Trudler, Swagata Ghatak, Michael Bula, et al. Dysregulation of miRNA expression and excitation in MEF2C autism patient hiPSC-neurons and cerebral organoids. Molecular Psychiatry. 2024:1-18. doi:10.1038/s41380-024-02761-9
Autism spectrum disorders
1.
Xiaoyu Chen, Fikri Birey, Min-Yin Li, et al. Antisense oligonucleotide therapeutic approach for Timothy syndrome. Nature. 2024;628(8009):818-825. doi:10.1038/s41586-024-07310-6