TY - JOUR KW - AAV vectors KW - gene therapy KW - human iPSC KW - organ-on-chip KW - retina on chip KW - retinal organoids AU - Kevin Achberger AU - Madalena Cipriano AU - Matthias J. Düchs AU - Christian Schön AU - Stefan Michelfelder AU - Birgit Stierstorfer AU - Thorsten Lamla AU - Stefan G. Kauschke AU - Johanna Chuchuy AU - Julia Roosz AU - Lena Mesch AU - Virginia Cora AU - Selin Pars AU - Natalia Pashkovskaia AU - Serena Corti AU - Sophia-Marie Hartmann AU - Alexander Kleger AU - Sebastian Kreuz AU - Udo Maier AU - Stefan Liebau AU - Peter Loskill BT - Stem Cell Reports DA - 2021-09-14 DO - 10.1016/j.stemcr.2021.08.008 IS - 9 LA - English PY - 2021 SP - 2242 EP - 2256 T2 - Stem Cell Reports TI - Human stem cell-based retina on chip as new translational model for validation of AAV retinal gene therapy vectors UR - https://www.cell.com/stem-cell-reports/abstract/S2213-6711(21)00426-4 VL - 16 Y2 - 2025-12-09 SN - 2213-6711 ER -