01270nas a2200457 4500000000100000000000100001008004100002260001500043653001600058653001700074653001500091653001800106653001900124653002200143100002000165700002200185700002300207700002100230700002400251700002400275700001900299700002300318700002000341700001600361700001500377700001800392700001500410700002500425700001700450700002600467700002100493700002000514700001400534700001800548700001800566245011900584856007400703300001400777490000700791022001400798 2021 d c2021-09-1410aAAV vectors10agene therapy10ahuman iPSC10aorgan-on-chip10aretina on chip10aretinal organoids1 aKevin Achberger1 aMadalena Cipriano1 aMatthias J. Düchs1 aChristian Schön1 aStefan Michelfelder1 aBirgit Stierstorfer1 aThorsten Lamla1 aStefan G. Kauschke1 aJohanna Chuchuy1 aJulia Roosz1 aLena Mesch1 aVirginia Cora1 aSelin Pars1 aNatalia Pashkovskaia1 aSerena Corti1 aSophia-Marie Hartmann1 aAlexander Kleger1 aSebastian Kreuz1 aUdo Maier1 aStefan Liebau1 aPeter Loskill00aHuman stem cell-based retina on chip as new translational model for validation of AAV retinal gene therapy vectors uhttps://www.cell.com/stem-cell-reports/abstract/S2213-6711(21)00426-4 a2242-22560 v16 a2213-6711